Induction of Fetal Hemoglobin by Gene Therapy

  • Walters, Mark C. M.D.

  • From the Blood and Marrow Transplant Program, University of California, San Francisco–Benioff Children's Hospital, Oakland.

Disclosure forms provided by the author are available with the full text of this editorial at NEJM.org.

New England Journal of Medicine 384(3):p 284-285, January 21, 2021. | DOI: 10.1056/NEJMe2034338

Corresponding Article

Post-Transcriptional Genetic Silencing ofBCL11Ato Treat Sickle Cell Disease

  • Esrick, Erica B. M.D.
  • Lehmann, Leslie E. M.D.
  • Biffi, Alessandra M.D., Ph.D.
  • Achebe, Maureen M.D.
  • Brendel, Christian Ph.D.
  • Ciuculescu, Marioara F. M.D.
  • Daley, Heather B.S.
  • MacKinnon, Brenda B.S.N., R.N.
  • Morris, Emily M.P.H.
  • Federico, Amy C.P.N.P.
  • Abriss, Daniela Ph.D.
  • Boardman, Kari B.S.
  • Khelladi, Radia B.S.
  • Shaw, Kit Ph.D.
  • Negre, Helene Ph.D.
  • Negre, Olivier Ph.D.
  • Nikiforow, Sarah M.D., Ph.D.
  • Ritz, Jerome M.D.
  • Pai, Sung-Yun M.D.
  • London, Wendy B. Ph.D.
  • Dansereau, Colleen M.S.N., R.N., C.P.N.
  • Heeney, Matthew M. M.D.
  • Armant, Myriam Ph.D.
  • Manis, John P M.D.
  • Williams, David A. M.D.
New England Journal of Medicine 384(3):p 205-215, January 21, 2021. | DOI: 10.1056/NEJMoa2029392

Corresponding Article

CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

  • Frangoul, Haydar M.D.
  • Altshuler, David M.D., Ph.D.
  • Cappellini, Domenica M. M.D.
  • Chen, Yi-Shan Ph.D.
  • Domm, Jennifer M.D.
  • Eustace, Brenda K. Ph.D.
  • Foell, Juergen M.D.
  • de la Fuente, Josu M.D., Ph.D.
  • Grupp, Stephan M.D., Ph.D.
  • Handgretinger, Rupert M.D.
  • Ho, Tony W. M.D.
  • Kattamis, Antonis M.D.
  • Kernytsky, Andrew Ph.D.
  • Lekstrom-Himes, Julie M.D.
  • Li, Amanda M. M.D.
  • Locatelli, Franco M.D.
  • Mapara, Markus Y. M.D., Ph.D.
  • de Montalembert, Mariane M.D.
  • Rondelli, Damiano M.D.
  • Sharma, Akshay M.B., B.S.
  • Sheth, Sujit M.D.
  • Soni, Sandeep M.D.
  • Steinberg, Martin H. M.D.
  • Wall, Donna M.D.
  • Yen, Angela Ph.D.
  • Corbacioglu, Selim M.D.
New England Journal of Medicine 384(3):p 252-260, January 21, 2021. | DOI: 10.1056/NEJMoa2031054
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