Gene Therapy Corrects Sickle Cell Disease in Mice

  • Komaroff, Anthony L. MD
NEJM Journal Watch :p JW200112250000004, 2002. | DOI: 10.1056/JW200112250000004

The single point mutation that causes sickle cell disease (SCD) has long been a target for gene therapy -- thus far, however, no therapy has …

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